The Healey & AMG Center is committed to communicating news and updates about Expanded Access Protocols (EAPs).

For the most recent EAP updates, read our latest EAP newsletter.

Upcoming EAP Webinars

The Healey & AMG Center hosts public Q&A webinars for the ALS community. Join us at 5:00-5:30pm Eastern Time on the second Thursday of each month to discuss news and updates about Expanded Access, ask questions, and hear from doctors and industry professionals at MGH and beyond.
  • Thursday, November 14th, 5:00 pm EST: Monthly EAP Discussion featuring Dr. David Walk and Never Surrender - Click here to register

Click here to register for upcoming webinars

Webinar Recordings

Featured EAP Webinars
October 10, 2024: Pridopidine EAP Update with Prilenia Therapeutics 
Suma Babu, MBBS, MPH of Massachusetts General Hospital was joined by Michael Hayden, MBChB, PhD, Chief Executive Officer of Prilenia Therapeutics, to discuss news and updates about Pridopidine, the investigational product studied in Regimen D of the HEALEY ALS Platform Trial, and answer questions from the audience. 
Watch Recording 

January 25, 2024: CNM-Au8 Update and Q&A with Clene Nanomedicine
Sabrina Paganoni, MD, PhD of Massachusetts General Hospital was joined by Jinsy Andrews, MD, MSc of Columbia University and Karen Ho, PhD from Clene Nanomedicine to discuss news and updates about CNM-Au8, the investigational product studied in Regimen C of the HEALEY ALS Platform Trial, and answer questions from the audience.
Watch Recording

May 14, 2021: NEALS 2021 ALS Drug Development Webinar Series: Site Considerations
Drs. Suma Babu and Katherine Nicholson discuss some of the issues faced by sites in a clinical trial including the specific steps and resources a site needs to open and run a clinical trial and an expanded access program.
Watch Recording
Monthly EAP Updates
October 10, 2024: Pridopidine EAP Update with Prilenia Therapeutics 
Suma Babu, MBBS, MPH of Massachusetts General Hospital was joined by Michael Hayden, MBChB, PhD, Chief Executive Officer of Prilenia Therapeutics, to discuss news and updates about Pridopidine, the investigational product studied in Regimen D of the HEALEY ALS Platform Trial, and answer questions from the audience. 
Watch Recording | Download Slides

September 12, 2024: EAP Update with Dr. Suma Babu
Suma Babu, MBBS, MPH of Massachusetts General Hospital presented news and updates about Expanded Access in the field of ALS research. Dr. Babu provided an overview of ongoing and upcoming Expanded Access Protocols (EAPs), including the Pridopidine EAP and RAPA-501 EAP, and answered questions from the audience.

August 8, 2024: EAP Discussion with Dr. Namita Goyal and Amanda Stevens
Suma Babu, MBBS, MPH of Massachusetts General Hospital was joined by guest speakers Dr. Namita Goyal from the University of California Irvine and Amanda Stevens from the axeALS Foundation to discuss collaborative efforts to build more Expanded Access Programs and EAP opportunities throughout the USA. 
Watch Recording | Download Slides

July 11, 2024: EAP Discussion with Patient Advisory Committee Members
Sabrina Paganoni, MD, PhD of Massachusetts General Hospital was joined by guest speakers Lauren Webb, LCSW and Steve Kowalski to discuss their perspective on Expanded Access Protocols (EAPs) and hear about their advocacy efforts as members of the EAP Patient Advisory Committee. The discussion highlighted online resources to learn more about EAPs and research opportunities in the ALS space.
Watch Recording | Download Slides

June 13, 2024: RAPA-501 EAP Discussion with Dr. James Berry
James Berry, MD, MPH of Massachusetts General Hospital presented updates about Expanded Access in the field of ALS research. Dr. Berry outlined the science behind an investigational product called RAPA-501, provided an overview of the RAPA-501 Expanded Access Protocol (EAP), and answered questions from the audience.
Watch RecordingDownload Slides

May 9, 2024: EAP Discussion with Shawn Sarbacker and Dr. Hristelina Ilieva
Sabrina Paganoni, MD, PhD, of Massachusetts General Hospital was joined by Shawn Sarbacker (founder of TechVSALS) and Hristelina Ilieva, MD, PhD of Thomas Jefferson University to discuss news and updates about Expanded Access in the field of ALS research.
Watch RecordingDownload Slides

April 18, 2024: Expanded Access and Patient Navigation
Sabrina Paganoni, MD, PhD of Massachusetts General Hospital was joined by Patient Navigators Catherine Small and Allison Bulat, along with Research Access Nurse Judi Carey, to discuss Expanded Access and answer questions from the audience. This week, we provided an overview of four newly launched webpages and highlighted online resources to learn more about Expanded Access Protocols (EAPs). 
Watch Recording | Download Slides

March 14, 2024: EAP Discussion with Dr. Jinsy Andrews
Sabrina Paganoni, MD, PhD, of Massachusetts General Hospital was joined by Jinsy Andrews, MD, Msc, FAAN, FANA, of Columbia University to discuss news and updates about Expanded Access in the field of ALS research. Dr. Andrews provided an overview about Expanded Access, outlined plans for Clene Nanomedicine's upcoming NIH-funded EAP for CNM-Au8, and answered questions from the audience. 
Watch Recording

February 8, 2024: EAP Discussion with Dr. Rick Bedlack and Gwen Petersen 

Sabrina Paganoni, MD, PhD, of Massachusetts General Hospital was joined by Richard Bedlack, MD, PhD, MS of Duke University and Patient Advocate Gwen Petersen to discuss progress and ongoing initiatives for Expanded Access in the field of ALS research. The guest speakers shared their experiences advocating for EAPs and answered questions from the audience.
Watch Recording

January 18, 2024: Pridopidine Update and Q&A with Prilenia Therapeutics
Sabrina Paganoni, MD, PhD of Massachusetts General Hospital was joined by Michael Hayden, MBChB, PhD, Chief Executive Officer of Prilenia Therapeutics, to discuss news and updates about Pridopidine, the investigational product studied in Regimen D of the HEALEY ALS Platform Trial, and answer questions from the audience.
Watch Recording

January 11, 2024:
Expanded Access Discussion with Amy Tsou, MD, MSc of the NIH
Sabrina Paganoni, MD, PhD, and Suma Babu, MBBS, MPH, of Massachusetts General Hospital were joined by Amy Tsou, MD, MSc and other guest speakers from the National Institute of Neurological Disorders and Stroke (NINDS) to discuss news and updates about Expanded Access in the field of ALS research. Dr. Tsou provided an overview of ongoing Expanded Access initiatives and answered questions from the audience. 
Watch Recording

December 14, 2023: EAP Update with James Berry, MD, MPH
James Berry, MD, MPH and Merit Cudkowicz, MD, MSc of Massachusetts General Hospital presented news and updates about Expanded Access in the field of ALS research. Dr. Berry provided an overview of ongoing and upcoming Expanded Access Protocols (EAPs) happening in parallel with the HEALEY ALS Platform Trial, and answered questions from the audience. 
Watch Recording

November 9, 2023: EAP Update with Suma Babu, MBBS, MPH
Suma Babu, MBBS,MPH of Massachusetts General Hospital presented news and updates about Expanded Access in the field of ALS research. Dr. Babu provided an overview of ongoing and upcoming Expanded Access Protocols happening in parallel to the HEALEY ALS Platform Trial, and answered questions from the audience. 
Watch Recording

September 28, 2023: EAP Update with Sabrina Paganoni, MD, PhD
Sabrina Paganoni, MD, PhD of Massachusetts General Hospital presented updates on the HEALEY ALS Platform Trial and answered questions from the audience. This week, the conversation focused on updates about Expanded Access progress and initiatives. 
Watch Recording

Press Releases

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